Are you or your child a patient with maple syrup urine syndrome or isovaleric acidemia?
Would you or your child like to participate in clinical trials owned and managed by our for-profit branch, Darling Therapeutics?
Would you like to have a say in your healthcare and your health equality rights?
We're recruiting 4 patients with maple syrup urine syndrome and 4 patients with isovaleric acidemia for P1/P2 and P3 trials run by Darling Therapeutics.  Everything will be free of charge: medication, transportation, accommodation, and meals.  We believe a one-time gene therapy approach is superior to alternatives!
Are you interested in learning more?
Email for more information.
NB we are no longer participating in PKU gene therapy due to BioMarin's efforts.
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