Are you or your child a patient with maple syrup urine syndrome or isovaleric acidemia?
Would you or your child like to participate in clinical trials owned and managed by our for-profit branch, Darling Therapeutics?
Would you like to have a say in your healthcare and your health equality rights?
We're recruiting 4 patients with maple syrup urine syndrome and 4 patients with isovaleric acidemia for P1/P2 and P3 trials run by Darling Therapeutics.  Everything will be free of charge: medication, transportation, accommodation, and meals.  We believe a one-time gene therapy approach is superior to alternatives!
Are you interested in learning more?
Email mkaura@dermetel.org for more information.
NB we are no longer participating in PKU gene therapy due to BioMarin's efforts.
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